Cross-Correction in HSC Gene Therapy for Metachromatic Leukodystrophy

Scritto il 29/07/2026
da Vasco MeneghiniValeria CalbiFilippo CasaliniIRCCS San Raffaele Scientific Institute, MilanElisabeth MangiameliSan Raffaele Telethon Institute for Gene Therapy, MilanFrancesco MorenaLink Campus University, RomeMarco PiccoliIRCCS Policlinico San Donato, San Donato Milanese, ItalyIlaria LafaceIRCCS San Raffaele Scientific Institute, MilanIlaria RossomannoFrancesca OrnaghiSan Raffaele Telethon Institute for Gene Therapy, MilanAndrea GhiroldiIRCCS Policlinico San Donato, San Donato Milanese, ItalyPaola M.V. RancoitaVita-Salute San Raffaele University, MilanFrancesca FumagalliIRCCS San Raffaele Scientific Institute, MilanSabata MartinoUniversity of Perugia, Perugia, ItalyLuigi AnastasiaVita-Salute San Raffaele University, MilanLuigi NaldiniAlessandro AiutiAngela GrittiSan Raffaele Telethon Institute for Gene Therapy, Milan

New England Journal of Medicine, Volume 395, Issue 5, Page 508-511, July 30, 2026.