In Vivo Base Editing of PCSK9 with VERVE-102 for Hypercholesterolemia
Scritto il 25/05/2026
da Scott B. Vafai Jörg Täubel Thomas Ashdown Riyaz S. Patel Sadaf Diamondali Jaimini Cegla Handrean Soran Bilal Bashir Alexander Abitbol Daniel Gaudet Alex Lauzière Liam R. Brunham David E. Newby Stephen J. Nicholls Russell S. Scott Jane Kerr Jean-Claude Tardif Catherine Lunken Steve E. Humphries Verena Karsten Patrick D. Tyler Xinyan Zhang Nidal Huniti Patrick A. Flight Chelsey L. Jensen Rick Falzone Joseph C. Biedenkapp Troy Lister Leslie E. Stolz Amit V. Khera and Sekar Kathiresan